Saturday, February 16, 2013

Targeted failure of the week. Post No 51-52. Xalkori, ABT-199 and any others

Let's start with Xalkori – I have already written that ALK-mutation is the key to success of the treatment... And what should do those who do not have this kind of mutation? And... guess what? According to the germans Xalkori does not work well even for those who do hav this mutation!!!

Germany's Institute for Quality and Efficiency in Health Care (IQWiG) said in a preliminary benefit assessment that Xalkori crizotinib from Pfizer Inc. (NYSE:PFE) provides "no additional benefit" over docetaxel or pemetrexed-containing chemotherapy in patients with previously treated, advanced non-small cell lung cancer (NSCLC) whose tumors are anaplastic lymphoma kinase (ALK)-positive -- Xalkori's approved indication. IQWiG said Xalkori may lead to improvements in health-related quality of life vs. the comparators requested by Germany's Federal Joint Committee (G-BA) in patients for whom chemotherapy is still an option. However, IQWIG said patients receiving Xalkori were at an increased risk for serious adverse events.
Because Pfizer's dossier did not include the requested data, IQWiG said Xalkori also has "no additional benefit" over G-BA's requested comparator of best supportive care (BSC) in patients for whom chemotherapy is no longer an option.
And the second failure is ABT-199, and not only this very targeted drug but other several candidates! It is a disaster for the company – to invest a huge amount of resources and time and then fail...
AbbVie Inc., the drug company that split off from Abbott Laboratories at the start of the year, suspended five studies on its experimental leukemia and lymphoma medicine after two patient deaths.
The patients died from tumor lysis syndrome, said Tracy Sorrentino, a spokeswoman for North Chicago, Illinois-based AbbVie. The complication stems from the rapid destruction of malignant cells after treatment that can trigger acute kidney failure. It occurs most often with large tumors such as those found in leukemia and lymphoma patients, according to the National Institutes of Health.
ABT-199 is one of the company’s most-promising new compounds and was slated to start the final round of testing usually required for U.S. regulatory approval this year.
“We have every expectation that these trials will come off the partial clinical hold and we’ll be able to initiate Phase 3 trials in 2013 as planned,” she said. “ABT-199 is a highly- potent agent and can result in the tumors reducing really quickly,” she said. “We are working to refine the dose.”

After the complication was discovered, AbbVie and its partner, Roche Holding AG, suspended the dose-escalation portion of the studies to determine the amount of drug that is safest and most effective, Sorrentino said. The risk stems from the drug’s potency and can be managed if the dose is carefully controlled, she said.

1 comment:

  1. You seriously miss the point about Xalkori. 60% of patients getting the drug at the metastatic state lived 12 months longer than the control group. That is hardly 'no effect'. The Germans don't like the fact that the patients still die after a year. So, what the Germans should have said is chemo kills patients faster and a whole lot cheaper than Xalkori. That is what this decision was based upon.

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